Question

The first clinical gene therapy was done for the treatment of

• A. $AIDS$
• B. canccystic fibrosis
• C. cystic fibrosis
• D. $SCID$ (Severe Combined Immuno Deficiency resulting form deficiency of $ADA$)

Answer 1

Answer: (D)

$SCID$ (Severe Combined Immuno Deficiency resulting form deficiency of $ADA$)

Answer 2

The first clinical gene therapy was given in $1990$ to a $4$-year old girl with adenosine deaminase $(ADA)$ deficiency. This enzyme is very important for the immune system to function. $ADA$ deficiency can lead to severe combined immune deficiency $(SCID)$.